Gene Therapy with Hematopoietic Stem Cells: The Diseased Bone Marrow's Point of View

Autor Cavazzana, Marina, Ribeil, Jean-Antoine, Lagresle-Peyrou, Chantal, André-Schmutz, Isabelle
Vydáno v Stem Cells Dev (2017)

Fetal consequences of maternal antiretroviral nucleoside reverse transcriptase inhibitor (NRTI) use in human and non-human primate pregnancy

Autor Poirier, Miriam C., Gibbons, Alexander T., Rugeles, Maria T., Andre-Schmutz, Isabelle, Blanche, Stephane
Vydáno v Curr Opin Pediatr (2015)

Gene Therapy for X-Linked Severe Combined Immunodeficiency: Where Do We Stand?

Autor Cavazzana, Marina, Six, Emmanuelle, Lagresle-Peyrou, Chantal, André-Schmutz, Isabelle, Hacein-Bey-Abina, Salima
Vydáno v Hum Gene Ther (2016)

A Nontoxic Transduction Enhancer Enables Highly Efficient Lentiviral Transduction of Primary Murine T Cells and Hematopoietic Stem Cells

Autor Delville, Marianne, Soheili, Tayebeh, Bellier, Florence, Durand, Amandine, Denis, Adeline, Lagresle-Peyrou, Chantal, Cavazzana, Marina, Andre-Schmutz, Isabelle, Six, Emmanuelle
Vydáno v Mol Ther Methods Clin Dev (2018)

Hematopoietic Stem Cell Transplant for the Treatment of X-MAID

Autor Henrickson, Sarah E., Andre-Schmutz, Isabelle, Lagresle-Peyrou, Chantal, Deardorff, Matthew A., Jyonouchi, Harumi, Neven, Benedicte, Bunin, Nancy, Heimall, Jennifer R.
Vydáno v Front Pediatr (2019)

CXCR4-Related Increase of Circulating Human Lymphoid Progenitors after Allogeneic Hematopoietic Stem Cell Transplantation

Autor Glauzy, Salomé, André-Schmutz, Isabelle, Larghero, Jérôme, Ezine, Sophie, de Latour, Régis Peffault, Moins-Teisserenc, Hélène, Servais, Sophie, Robin, Marie, Socié, Gérard, Clave, Emmanuel, Toubert, Antoine
Vydáno 2014

Comparing genotoxic signatures in cord blood cells from neonates exposed in utero to zidovudine or tenofovir

Autor Vivanti, Alexandre, Soheili, Tayebeh S., Cuccuini, Wendy, Luce, Sonia, Mandelbrot, Laurent, Lechenadec, Jerome, Cordier, Anne-Gael, Azria, Elie, Soulier, Jean, Cavazzana, Marina, Blanche, Stéphane, André-Schmutz, Isabelle
Vydáno v AIDS (2015)

Gene transfer into hematopoietic stem cells reduces HLH manifestations in a murine model of Munc13-4 deficiency

Autor Soheili, Tayebeh, Durand, Amandine, Sepulveda, Fernando E., Rivière, Julie, Lagresle-Peyrou, Chantal, Sadek, Hanem, de Saint Basile, Geneviève, Martin, Samia, Mavilio, Fulvio, Cavazzana, Marina, André-Schmutz, Isabelle
Vydáno v Blood Adv (2017)

A human postnatal lymphoid progenitor capable of circulating and seeding the thymus

Autor Six, Emmanuelle M., Bonhomme, Delphine, Monteiro, Marta, Beldjord, Kheira, Jurkowska, Monika, Cordier-Garcia, Corinne, Garrigue, Alexandrine, Dal Cortivo, Liliane, Rocha, Benedita, Fischer, Alain, Cavazzana-Calvo, Marina, André-Schmutz, Isabelle
Vydáno 2007

Human T-Lymphoid Progenitors Generated in a Feeder-Cell-Free Delta-Like-4 Culture System Promote T-Cell Reconstitution in NOD/SCID/γc(−/−) Mice

Autor Reimann, Christian, Six, Emmanuelle, Dal-Cortivo, Liliane, Schiavo, Andrea, Appourchaux, Kevin, Lagresle-Peyrou, Chantal, de Chappedelaine, Corinne, Ternaux, Brigitte, Coulombel, Laure, Beldjord, Kheira, Cavazzana-Calvo, Marina, Andre-Schmutz, Isabelle
Vydáno 2012

MST1 mutations in autosomal recessive primary immunodeficiency characterized by defective naive T-cell survival

Autor Nehme, Nadine T., Schmid, Jana Pachlopnik, Debeurme, Franck, André-Schmutz, Isabelle, Lim, Annick, Nitschke, Patrick, Rieux-Laucat, Frédéric, Lutz, Patrick, Picard, Capucine, Mahlaoui, Nizar, Fischer, Alain, de Saint Basile, Geneviève
Vydáno 2011

An Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Disease Phenotype

Autor Weber, Leslie, Poletti, Valentina, Magrin, Elisa, Antoniani, Chiara, Martin, Samia, Bayard, Charles, Sadek, Hanem, Felix, Tristan, Meneghini, Vasco, Antoniou, Michael N., El-Nemer, Wassim, Mavilio, Fulvio, Cavazzana, Marina, Andre-Schmutz, Isabelle, Miccio, Annarita
Vydáno v Mol Ther Methods Clin Dev (2018)

Generation of adult human T-cell progenitors for immunotherapeutic applications

Autor Simons, Laura, Ma, Kuiying, de Chappedelaine, Corinne, Moiranghtem, Ranjita Devi, Elkaim, Elodie, Olivré, Juliette, Susini, Sandrine, Appourchaux, Kevin, Reimann, Christian, Sadek, Hanem, Pellé, Olivier, Cagnard, Nicolas, Magrin, Elisa, Lagresle-Peyrou, Chantal, Taghon, Tom, Rausell, Antonio, Cavazzana, Marina, André-Schmutz, Isabelle
Vydáno v J Allergy Clin Immunol (2018)

Loss of ARHGEF1 causes a human primary antibody deficiency

Autor Bouafia, Amine, Lofek, Sébastien, Bruneau, Julie, Chentout, Loïc, Lamrini, Hicham, Trinquand, Amélie, Deau, Marie-Céline, Heurtier, Lucie, Meignin, Véronique, Picard, Capucine, Macintyre, Elizabeth, Alibeu, Olivier, Bras, Marc, Molina, Thierry Jo, Cavazzana, Marina, André-Schmutz, Isabelle, Durandy, Anne, Fischer, Alain, Oksenhendler, Eric, Kracker, Sven
Vydáno v J Clin Invest (2019)

Editing a γ-globin repressor binding site restores fetal hemoglobin synthesis and corrects the sickle cell disease phenotype

Autor Weber, Leslie, Frati, Giacomo, Felix, Tristan, Hardouin, Giulia, Casini, Antonio, Wollenschlaeger, Clara, Meneghini, Vasco, Masson, Cecile, De Cian, Anne, Chalumeau, Anne, Mavilio, Fulvio, Amendola, Mario, Andre-Schmutz, Isabelle, Cereseto, Anna, El Nemer, Wassim, Concordet, Jean-Paul, Giovannangeli, Carine, Cavazzana, Marina, Miccio, Annarita
Vydáno v Sci Adv (2020)

RUNX1-dependent RAG1 deposition instigates human TCR-δ locus rearrangement

Autor Cieslak, Agata, Le Noir, Sandrine, Trinquand, Amélie, Lhermitte, Ludovic, Franchini, Don-Marc, Villarese, Patrick, Gon, Stéphanie, Bond, Jonathan, Simonin, Mathieu, Vanhille, Laurent, Reimann, Christian, Verhoeyen, Els, Larghero, Jerome, Six, Emmanuelle, Spicuglia, Salvatore, André-Schmutz, Isabelle, Langerak, Anton, Nadel, Bertrand, Macintyre, Elizabeth, Payet-Bornet, Dominique, Asnafi, Vahid
Vydáno 2014

RUNX1-dependent RAG1 deposition instigates human TCR-δ locus rearrangement

Autor Cieslak, Agata, Le Noir, Sandrine, Trinquand, Amélie, Lhermitte, Ludovic, Franchini, Don-Marc, Villarese, Patrick, Gon, Stéphanie, Bond, Jonathan, Simonin, Mathieu, Vanhille, Laurent, Reimann, Christian, Verhoeyen, Els, Larghero, Jerome, Six, Emmanuelle, Spicuglia, Salvatore, André-Schmutz, Isabelle, Langerak, Anton, Nadel, Bertrand, Macintyre, Elizabeth, Payet-Bornet, Dominique, Asnafi, Vahid
Vydáno v J Exp Med (2014)

Plerixafor enables safe, rapid, efficient mobilization of hematopoietic stem cells in sickle cell disease patients after exchange transfusion

Autor Lagresle-Peyrou, Chantal, Lefrère, François, Magrin, Elisa, Ribeil, Jean-Antoine, Romano, Oriana, Weber, Leslie, Magnani, Alessandra, Sadek, Hanem, Plantier, Clémence, Gabrion, Aurélie, Ternaux, Brigitte, Félix, Tristan, Couzin, Chloé, Stanislas, Aurélie, Tréluyer, Jean-Marc, Lamhaut, Lionel, Joseph, Laure, Delville, Marianne, Miccio, Annarita, André-Schmutz, Isabelle, Cavazzana, Marina
Vydáno v Haematologica (2018)