Treatment of transthyretin (TTR) amyloid cardiomyopathy with an antisense oligonucleotide inhibitor of TTR synthesis

af Benson, Merrill D, Ackermann, Elizabeth J, Monia, Brett P
Udgivet i Orphanet J Rare Dis (2015)

Suppression of Vascular Endothelial Growth Factor-Mediated Endothelial Cell Protection by Survivin Targeting

af Mesri, Mehdi, Morales-Ruiz, Manuel, Ackermann, Elizabeth J., Bennett, C. Frank, Pober, Jordan S., Sessa, William C., Altieri, Dario C.
Udgivet 2001

Population Pharmacokinetic–Pharmacodynamic Modeling of Inotersen, an Antisense Oligonucleotide for Treatment of Patients with Hereditary Transthyretin Amyloidosis

af Yu, Rosie Z., Collins, Jon W., Hall, Shannon, Ackermann, Elizabeth J., Geary, Richard S., Monia, Brett P., Henry, Scott P., Wang, Yanfeng
Udgivet i Nucleic Acid Ther (2020)

Burden of hereditary transthyretin amyloidosis on quality of life

af Yarlas, Aaron, Gertz, Morie A., Dasgupta, Noel R., Obici, Laura, Pollock, Michael, Ackermann, Elizabeth J., Lovley, Andrew, Kessler, Asia Sikora, Patel, Pankaj A., White, Michelle K., Guthrie, Spencer D.
Udgivet i Muscle Nerve (2019)

Evaluation of Therapeutic Oligonucleotides for Familial Amyloid Polyneuropathy in Patient-Derived Hepatocyte-Like Cells

af Niemietz, Christoph J., Sauer, Vanessa, Stella, Jacqueline, Fleischhauer, Lutz, Chandhok, Gursimran, Guttmann, Sarah, Avsar, Yesim, Guo, Shuling, Ackermann, Elizabeth J., Gollob, Jared, Monia, Brett P., Zibert, Andree, Schmidt, Hartmut H. -J.
Udgivet i PLoS One (2016)

mNIS+7 and lower limb function in inotersen treatment of hereditary transthyretin‐mediated amyloidosis

af Dyck, P. James B., Kincaid, John C., Wiesman, Janice F., Polydefkis, Michael, Litchy, William J., Mauermann, Michelle L., Ackermann, Elizabeth J., Guthrie, Spencer, Pollock, Michael, Jung, Shiangtung W., Baker, Brenda F., Dyck, Peter J.
Udgivet i Muscle Nerve (2020)

Neuropathy symptom and change: Inotersen treatment of hereditary transthyretin amyloidosis

af Dyck, P. James B., Coelho, Teresa, Waddington Cruz, Marcia, Brannagan, Thomas H., Khella, Sami, Karam, Chafic, Berk, John L., Polydefkis, Michael J., Kincaid, John C., Wiesman, Janice F., Litchy, William J., Mauermann, Michelle L., Ackermann, Elizabeth J., Baker, Brenda F., Jung, Shiangtung W., Guthrie, Spencer, Pollock, Michael, Dyck, Peter J.
Udgivet i Muscle Nerve (2020)

Inotersen preserves or improves quality of life in hereditary transthyretin amyloidosis

af Coelho, Teresa, Yarlas, Aaron, Waddington-Cruz, Marcia, White, Michelle K., Sikora Kessler, Asia, Lovley, Andrew, Pollock, Michael, Guthrie, Spencer, Ackermann, Elizabeth J., Hughes, Steven G., Karam, Chafic, Khella, Sami, Gertz, Morie, Merlini, Giampaolo, Obici, Laura, Schmidt, Hartmut H., Polydefkis, Michael, Dyck, P. James B., Brannagan III, Thomas H., Conceição, Isabel, Benson, Merrill D., Berk, John L.
Udgivet i J Neurol (2019)

Assessing mNIS+7(Ionis) and International Neurologists’ Proficiency in a FAP Trial

af Dyck, Peter J., Kincaid, John C., Dyck, P. James B., Chaudhry, Vinay, Goyal, Namita A., Alves, Christina, Salhi, Hayet, Wiesman, Janice F., Labeyrie, Celine, Robinson-Papp, Jessica, Cardoso, Márcio, Laura, Matilde, Ruzhansky, Katherine, Cortese, Andrea, Brannagan, Thomas H., Khoury, Julie, Khella, Sami, Waddington-Cruz, Márcia, Ferreira, João, Wang, Annabel K., Pinto, Marcus V., Ayache, Samar S., Benson, Merrill D., Berk, John L., Coelho, Teresa, Polydefkis, Michael, Gorevic, Peter, Adams, David H., Plante-Bordeneuve, Violaine, Whelan, Carol, Merlini, Giampaolo, Heitner, Stephen, Drachman, Brian M., Conceição, Isabel, Klein, Christopher J., Gertz, Morie A., Ackermann, Elizabeth J., Hughes, Steven. G., Mauermann, Michelle. L., Bergemann, Rito, Lodermeier, Karen A., Davies, Jenny L., Carter, Rickey E., Litchy, William J.
Udgivet i Muscle Nerve (2017)