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Splicing mutation in TAZ gene leading to exon skipping and Barth syndrome

Barth syndrome is a monogenic X-linked disorder characterized by cardiomyopathy, skeletal myopathy and neutropenia. It is caused by deficiency of cardiolipin and associated with mutations in the tafazzin gene (TAZ). A 3 years old boy with dilated cardiomyopathy, neutropenia and growth retardation wa...

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Bibliografski detalji
Izdano u:Acta Myol
Glavni autori: Sivitskaya, Larysa, Danilenko, Nina, Motuk, Iryna, Zhelev, Nikolai
Format: Artigo
Jezik:Inglês
Izdano: Pacini Editore Srl 2021
Teme:
Online pristup:https://ncbi.nlm.nih.gov/pmc/articles/PMC8290511/
https://ncbi.nlm.nih.gov/pubmed/34355125
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.36185/2532-1900-047
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