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Sequential everolimus for angiomyolipoma associated with tuberous sclerosis complex: a prospective cohort study

BACKGROUND: To evaluate the efficacy, safety and health economics of sequential everolimus in treating angiomyolipoma (AML) associated with tuberous sclerosis complex (TSC). METHODS: In this prospective cohort study, patients met the inclusion criteria received standard or sequential treatment accor...

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Pubblicato in:Orphanet J Rare Dis
Autori principali: Gu, Liangyou, Peng, Cheng, Zhang, Fan, Fang, Cunjin, Guo, Gang
Natura: Artigo
Lingua:Inglês
Pubblicazione: BioMed Central 2021
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC8201725/
https://ncbi.nlm.nih.gov/pubmed/34127034
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-021-01913-2
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