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Managing challenging pain and irritability in OSTM1 mutation-related infantile malignant osteopetrosis

Osteopetrosis describes a heterogeneous group of diseases characterised by increased bone density due to impaired osteoclast. The malignant infantile autosomal recessive (MIOP) form caused by mutations in OSTM1 is the most severe form of osteopetrosis. Children with this phenotype exhibit multisyste...

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Detalhes bibliográficos
Publicado no:BMJ Case Rep
Main Authors: Alotaibi, Qutaibah, Dighe, Manjiri
Formato: Artigo
Idioma:Inglês
Publicado em: BMJ Publishing Group 2021
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC8137230/
https://ncbi.nlm.nih.gov/pubmed/34011644
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1136/bcr-2021-242498
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