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Managing challenging pain and irritability in OSTM1 mutation-related infantile malignant osteopetrosis

Osteopetrosis describes a heterogeneous group of diseases characterised by increased bone density due to impaired osteoclast. The malignant infantile autosomal recessive (MIOP) form caused by mutations in OSTM1 is the most severe form of osteopetrosis. Children with this phenotype exhibit multisyste...

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Dades bibliogràfiques
Publicat a:BMJ Case Rep
Autors principals: Alotaibi, Qutaibah, Dighe, Manjiri
Format: Artigo
Idioma:Inglês
Publicat: BMJ Publishing Group 2021
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC8137230/
https://ncbi.nlm.nih.gov/pubmed/34011644
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1136/bcr-2021-242498
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