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Managing challenging pain and irritability in OSTM1 mutation-related infantile malignant osteopetrosis

Osteopetrosis describes a heterogeneous group of diseases characterised by increased bone density due to impaired osteoclast. The malignant infantile autosomal recessive (MIOP) form caused by mutations in OSTM1 is the most severe form of osteopetrosis. Children with this phenotype exhibit multisyste...

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Pubblicato in:BMJ Case Rep
Autori principali: Alotaibi, Qutaibah, Dighe, Manjiri
Natura: Artigo
Lingua:Inglês
Pubblicazione: BMJ Publishing Group 2021
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC8137230/
https://ncbi.nlm.nih.gov/pubmed/34011644
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1136/bcr-2021-242498
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