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Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm

This expert opinion originally developed by a panel of the Italian Society of Thalassemias and Hemoglobinopathies (SITE), reviewed and adopted by the European Hematology Association (EHA) through the EHA Scientific Working Group on Red Cells and Iron, has been developed as priority decision-making a...

Täydet tiedot

Tallennettuna:
Bibliografiset tiedot
Julkaisussa:Hemasphere
Päätekijät: Baronciani, Donatella, Casale, Maddalena, De Franceschi, Lucia, Graziadei, Giovanna, Longo, Filomena, Origa, Raffaella, Rigano, Paolo, Pinto, Valeria, Marchetti, Monia, Gigante, Antonia, Iolascon, Achille, Forni, Gian Luca
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: Lippincott Williams & Wilkins 2021
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC8096466/
https://ncbi.nlm.nih.gov/pubmed/33969274
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1097/HS9.0000000000000555
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