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Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm

This expert opinion originally developed by a panel of the Italian Society of Thalassemias and Hemoglobinopathies (SITE), reviewed and adopted by the European Hematology Association (EHA) through the EHA Scientific Working Group on Red Cells and Iron, has been developed as priority decision-making a...

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Dettagli Bibliografici
Pubblicato in:Hemasphere
Autori principali: Baronciani, Donatella, Casale, Maddalena, De Franceschi, Lucia, Graziadei, Giovanna, Longo, Filomena, Origa, Raffaella, Rigano, Paolo, Pinto, Valeria, Marchetti, Monia, Gigante, Antonia, Iolascon, Achille, Forni, Gian Luca
Natura: Artigo
Lingua:Inglês
Pubblicazione: Lippincott Williams & Wilkins 2021
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC8096466/
https://ncbi.nlm.nih.gov/pubmed/33969274
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1097/HS9.0000000000000555
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