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Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm

This expert opinion originally developed by a panel of the Italian Society of Thalassemias and Hemoglobinopathies (SITE), reviewed and adopted by the European Hematology Association (EHA) through the EHA Scientific Working Group on Red Cells and Iron, has been developed as priority decision-making a...

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Detalhes bibliográficos
Publicado no:Hemasphere
Main Authors: Baronciani, Donatella, Casale, Maddalena, De Franceschi, Lucia, Graziadei, Giovanna, Longo, Filomena, Origa, Raffaella, Rigano, Paolo, Pinto, Valeria, Marchetti, Monia, Gigante, Antonia, Iolascon, Achille, Forni, Gian Luca
Formato: Artigo
Idioma:Inglês
Publicado em: Lippincott Williams & Wilkins 2021
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC8096466/
https://ncbi.nlm.nih.gov/pubmed/33969274
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1097/HS9.0000000000000555
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