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CRISPR/Cas9 gene editing for curing sickle cell disease

Sickle cell disease (SCD) is the most common monogenic blood disorder marked by severe pain, end-organ damage, and early mortality. Treatment options for SCD remain very limited. There are only four FDA approved drugs to reduce acute complications. The only curative therapy for SCD is hematopoietic...

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Dades bibliogràfiques
Publicat a:Transfus Apher Sci
Autors principals: Park, So Hyun, Bao, Gang
Format: Artigo
Idioma:Inglês
Publicat: 2021
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC8049447/
https://ncbi.nlm.nih.gov/pubmed/33455878
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.transci.2021.103060
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