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Proof-of-Concept: Antisense Oligonucleotide Mediated Skipping of Fibrillin-1 Exon 52

Marfan syndrome is one of the most common dominantly inherited connective tissue disorders, affecting 2–3 in 10,000 individuals, and is caused by one of over 2800 unique FBN1 mutations. Mutations in FBN1 result in reduced fibrillin-1 expression, or the production of two different fibrillin-1 monomer...

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Détails bibliographiques
Publié dans:Int J Mol Sci
Auteurs principaux: Cale, Jessica M., Greer, Kane, Fletcher, Sue, Wilton, Steve D.
Format: Artigo
Langue:Inglês
Publié: MDPI 2021
Sujets:
Accès en ligne:https://ncbi.nlm.nih.gov/pmc/articles/PMC8037683/
https://ncbi.nlm.nih.gov/pubmed/33801742
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms22073479
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