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Delivery of Tissue-Targeted Scalpels: Opportunities and Challenges for in Vivo CRISPR/Cas-Based Genome Editing

CRISPR/Cas9-based genome editing has quickly emerged as a powerful breakthrough technology for use in diverse settings across biomedical research and therapeutic development. Recent efforts toward understanding gene modification methods in vitro have led to substantial improvements in ex vivo genome...

Ausführliche Beschreibung

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Bibliographische Detailangaben
Veröffentlicht in:ACS Nano
Hauptverfasser: Wei, Tuo, Cheng, Qiang, Farbiak, Lukas, Anderson, Daniel G., Langer, Robert, Siegwart, Daniel J.
Format: Artigo
Sprache:Inglês
Veröffentlicht: 2020
Schlagworte:
Online Zugang:https://ncbi.nlm.nih.gov/pmc/articles/PMC7996671/
https://ncbi.nlm.nih.gov/pubmed/32697075
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1021/acsnano.0c04707
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