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Autosomal dominant neuronal ceroid lipofuscinosis: Clinical features and molecular basis

The neuronal ceroid lipofuscinoses (NCLs) are at least 13 distinct progressive neurodegenerative disorders unified by the accumulation of lysosomal auto-fluorescent material called lipofuscin. The only form that occurs via autosomal-dominant inheritance exhibits adult onset and is sometimes referred...

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Detalhes bibliográficos
Publicado no:Clin Genet
Main Authors: Naseri, Nima, Sharma, Manu, Velinov, Milen
Formato: Artigo
Idioma:Inglês
Publicado em: 2020
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7899141/
https://ncbi.nlm.nih.gov/pubmed/32783189
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1111/cge.13829
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