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Cell Transplantation Combined with Recombinant Collagen Peptides for the Treatment of Fabry Disease

Fabry disease is caused by a decrease in or loss of the activity of alpha-galactosidase, which causes its substrates globotriaosylceramide (Gb3) and globotriaosylsphingosine (lyso-Gb3) to accumulate in cells throughout the body. This accumulation results in progressive kidney injury due to glomerulo...

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Publicat a:Cell Transplant
Autors principals: Kami, Daisuke, Yamanami, Masashi, Tsukimura, Takahiro, Maeda, Hideki, Togawa, Tadayasu, Sakuraba, Hitoshi, Gojo, Satoshi
Format: Artigo
Idioma:Inglês
Publicat: SAGE Publications 2020
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC7873760/
https://ncbi.nlm.nih.gov/pubmed/33300391
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1177/0963689720976362
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