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Detection of novel Fabry disease‐associated pathogenic variants in Japanese patients by newborn and high‐risk screening

BACKGROUND: In Japan, newborn and high‐risk screening for Fabry disease (FD), an inherited X‐linked disorder caused by GLA mutations, using dried blood spots was initiated in 2006. In newborn screening, 599,711 newborns were screened by December 2018, and 57 newborns from 54 families with 26 FD‐asso...

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Publicat a:Mol Genet Genomic Med
Autors principals: Sawada, Takaaki, Kido, Jun, Sugawara, Keishin, Matsumoto, Shirou, Takada, Fumio, Tsuboi, Kazuya, Ohtake, Akira, Endo, Fumio, Nakamura, Kimitoshi
Format: Artigo
Idioma:Inglês
Publicat: John Wiley and Sons Inc. 2020
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC7667298/
https://ncbi.nlm.nih.gov/pubmed/33016649
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/mgg3.1502
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