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Treosulfan Exposure Predicts Thalassemia-Free Survival in Patients with Beta Thalassemia Major Undergoing Allogeneic Hematopoietic Cell Transplantation

A toxicity-reduced conditioning regimen with treosulfan, fludarabine, and thiotepa in patients with high-risk β-thalassemia major has significantly improved hematopoietic stem cell transplantation (HCT) outcomes. However, complications resulting from regimen-related toxicities (RRTs), mixed chimeris...

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Библиографические подробности
Опубликовано в: :Clin Pharmacol Ther
Главные авторы: Pai, Aswin Anand, Mohanan, Ezhilpavai, Panetta, John C., Kulkarni, Uday P., Illangeswaran, Raveen Stephen Stallon, Balakrishnan, Balaji, Jayaraman, Agila, Edison, Eunice S., Lakshmi, Kavitha M., Devasia, Anup J., Fouzia, Nambiathayil Aboobacker, Korula, Anu, Abraham, Aby, George, Biju, Srivastava, Alok, Mathews, Vikram, Standing, Joseph F., Balasubramanian, Poonkuzhali
Формат: Artigo
Язык:Inglês
Опубликовано: 2024
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC7615782/
https://ncbi.nlm.nih.gov/pubmed/37846495
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/cpt.3078
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