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How I manage patients with Wiskott Aldrich syndrome

Wiskott Aldrich syndrome (WAS) is a primary immunodeficiency disease resulting in recurrent infections, eczema and microthrombocytopaenia. In its classical form, significant combined immune deficiency, autoimmune complications and risk of haematological malignancy necessitate early correction with s...

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Détails bibliographiques
Publié dans:Br J Haematol
Auteurs principaux: Rivers, Elizabeth, Worth, Austen, Thrasher, Adrian J., Burns, Siobhan O.
Format: Artigo
Langue:Inglês
Publié: 2019
Sujets:
Accès en ligne:https://ncbi.nlm.nih.gov/pmc/articles/PMC7612067/
https://ncbi.nlm.nih.gov/pubmed/30864154
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1111/bjh.15831
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