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A novel deep intronic variant in ATP7B in five unrelated families affected by Wilson disease

BACKGROUND: Wilson disease is an autosomal recessive metabolic disorder resulting from accumulation of excess copper especially in the liver and brain. This disease is mainly characterized by hepatic disorders and less frequently by neuro‐psychiatric disturbances. This recessive disease is due to mu...

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Detaylı Bibliyografya
Yayımlandı:Mol Genet Genomic Med
Asıl Yazarlar: Woimant, France, Poujois, Aurelia, Bloch, Adrien, Jordi, Tabaras, Laplanche, Jean‐Louis, Morel, Hélène, Collet, Corinne
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: John Wiley and Sons Inc. 2020
Konular:
Online Erişim:https://ncbi.nlm.nih.gov/pmc/articles/PMC7549599/
https://ncbi.nlm.nih.gov/pubmed/32770663
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/mgg3.1428
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