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A novel deep intronic variant in ATP7B in five unrelated families affected by Wilson disease

BACKGROUND: Wilson disease is an autosomal recessive metabolic disorder resulting from accumulation of excess copper especially in the liver and brain. This disease is mainly characterized by hepatic disorders and less frequently by neuro‐psychiatric disturbances. This recessive disease is due to mu...

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Detalhes bibliográficos
Publicado no:Mol Genet Genomic Med
Main Authors: Woimant, France, Poujois, Aurelia, Bloch, Adrien, Jordi, Tabaras, Laplanche, Jean‐Louis, Morel, Hélène, Collet, Corinne
Formato: Artigo
Idioma:Inglês
Publicado em: John Wiley and Sons Inc. 2020
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7549599/
https://ncbi.nlm.nih.gov/pubmed/32770663
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/mgg3.1428
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