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Effective Dystrophin Restoration by a Novel Muscle-Homing Peptide-Morpholino Conjugate in Dystrophin-Deficient mdx Mice

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Bibliografske podrobnosti
izdano v:Mol Ther
Main Authors: Gao, Xianjun, Zhao, Jingwen, Han, Gang, Zhang, Yajie, Dong, Xue, Cao, Limin, Wang, Qingsong, Moulton, Hong M., Yin, HaiFang
Format: Artigo
Jezik:Inglês
Izdano: American Society of Gene & Cell Therapy 2020
Teme:
Online dostop:https://ncbi.nlm.nih.gov/pmc/articles/PMC7545002/
https://ncbi.nlm.nih.gov/pubmed/32888401
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymthe.2020.08.020
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