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RNA in spinal muscular atrophy: therapeutic implications of targeting

INTRODUCTION: Spinal muscular atrophy (SMA) is caused by low levels of the Survival Motor Neuron (SMN) protein due to deletions of or mutations in the SMN1 gene. Humans carry another nearly identical gene, SMN2, which mostly produces a truncated and less stable protein SMNΔ7 due to predominant skipp...

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Bibliografske podrobnosti
izdano v:Expert Opin Ther Targets
Main Authors: Singh, Ravindra N., Seo, Joonbae, Singh, Natalia N.
Format: Artigo
Jezik:Inglês
Izdano: 2020
Teme:
Online dostop:https://ncbi.nlm.nih.gov/pmc/articles/PMC7529864/
https://ncbi.nlm.nih.gov/pubmed/32538213
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1080/14728222.2020.1783241
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