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Utility of microminipigs for evaluating liver-mediated gene expression in the presence of neutralizing antibody against vector capsid

Adeno-associated virus (AAV) vectors can transduce hepatocytes efficiently in vivo in various animal species, including humans. Few reports, however, have examined the utility of pigs in gene therapy. Pigs are potentially useful in preclinical studies because of their anatomical and physiological si...

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Detalhes bibliográficos
Publicado no:Gene Ther
Main Authors: Watano, Ryota, Ohmori, Tsukasa, Hishikawa, Shuji, Sakata, Asuka, Mizukami, Hiroaki
Formato: Artigo
Idioma:Inglês
Publicado em: Nature Publishing Group UK 2020
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7500982/
https://ncbi.nlm.nih.gov/pubmed/32066928
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41434-020-0125-0
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