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An artificial cationic oligosaccharide combined with phosphorothioate linkages strongly improves siRNA stability

Small interfering RNAs (siRNAs) are potential tools for gene-silencing therapy, but their instability is one of the obstacles in the development of siRNA-based drugs. To improve siRNA stability, we synthesised a double-stranded RNA-binding cationic oligodiaminogalactose 4mer (ODAGal4) and investigat...

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Pubblicato in:Sci Rep
Autori principali: Irie, Atsushi, Sato, Kazuki, Hara, Rintaro Iwata, Wada, Takeshi, Shibasaki, Futoshi
Natura: Artigo
Lingua:Inglês
Pubblicazione: Nature Publishing Group UK 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7481297/
https://ncbi.nlm.nih.gov/pubmed/32908235
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41598-020-71896-w
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