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Gorham-Stout disease successfully treated with sirolimus (rapamycin): a case report and review of the literature

BACKGROUND: Gorham-Stout disease (GSD) is a rare disease characterized by bone lesions and osteolysis. Therapy usually involves surgical resection. Sirolimus (Rapamycin) is used in some patients with GSD but the efficacy and safety of Sirolimus remains unclear. We propose that Sirolimus may be a nov...

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Dettagli Bibliografici
Pubblicato in:BMC Musculoskelet Disord
Autori principali: Liang, Yu, Tian, Ruicheng, Wang, Jing, Shan, Yuhua, Gao, Hongxiang, Xie, Chenjie, Li, Jingjing, Xu, Min, Gu, Song
Natura: Artigo
Lingua:Inglês
Pubblicazione: BioMed Central 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7446191/
https://ncbi.nlm.nih.gov/pubmed/32843029
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s12891-020-03540-7
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