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Gorham-Stout disease successfully treated with sirolimus (rapamycin): a case report and review of the literature

BACKGROUND: Gorham-Stout disease (GSD) is a rare disease characterized by bone lesions and osteolysis. Therapy usually involves surgical resection. Sirolimus (Rapamycin) is used in some patients with GSD but the efficacy and safety of Sirolimus remains unclear. We propose that Sirolimus may be a nov...

Täydet tiedot

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Bibliografiset tiedot
Julkaisussa:BMC Musculoskelet Disord
Päätekijät: Liang, Yu, Tian, Ruicheng, Wang, Jing, Shan, Yuhua, Gao, Hongxiang, Xie, Chenjie, Li, Jingjing, Xu, Min, Gu, Song
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: BioMed Central 2020
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC7446191/
https://ncbi.nlm.nih.gov/pubmed/32843029
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s12891-020-03540-7
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