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Gorham-Stout disease successfully treated with sirolimus (rapamycin): a case report and review of the literature

Abstract Background Gorham-Stout disease (GSD) is a rare disease characterized by bone lesions and osteolysis. Therapy usually involves surgical resection. Sirolimus (Rapamycin) is used in some patients with GSD but the efficacy and safety of Sirolimus remains unclear. We propose that Sirolimus may...

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Autori principali: Yu Liang, Ruicheng Tian, Jing Wang, Yuhua Shan, Hongxiang Gao, Chenjie Xie, Jingjing Li, Min Xu, Song Gu
Natura: Artigo
Lingua:Inglês
Pubblicazione: BMC 2020-08-01
Serie:BMC Musculoskeletal Disorders
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Accesso online:http://link.springer.com/article/10.1186/s12891-020-03540-7
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