Loading...

Limited time window for retinal gene therapy in a preclinical model of ciliopathy

Retinal degeneration is a common clinical feature of ciliopathies, a group of genetic diseases linked to ciliary dysfunction, and gene therapy is an attractive treatment option to prevent vision loss. Although the efficacy of retinal gene therapy is well established by multiple proof-of-concept prec...

Fuld beskrivelse

Na minha lista:
Bibliografiske detaljer
Udgivet i:Hum Mol Genet
Main Authors: Datta, Poppy, Ruffcorn, Avri, Seo, Seongjin
Format: Artigo
Sprog:Inglês
Udgivet: Oxford University Press 2020
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC7424757/
https://ncbi.nlm.nih.gov/pubmed/32568387
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddaa124
Tags: Tilføj Tag
Ingen Tags, Vær først til at tagge denne postø!