Nalaganje...

Benefits of Prophylactic Short-Course Immune Tolerance Induction in Patients With Infantile Pompe Disease: Demonstration of Long-Term Safety and Efficacy in an Expanded Cohort

Immune tolerance induction (ITI) with a short-course of rituximab, methotrexate, and/or IVIG in the enzyme replacement therapy (ERT)-naïve setting has prolonged survival and improved clinical outcomes in patients with infantile Pompe disease (IPD) lacking endogenous acid-alpha glucosidase (GAA), kno...

Popoln opis

Shranjeno v:
Bibliografske podrobnosti
izdano v:Front Immunol
Main Authors: Desai, Ankit K., Baloh, Carolyn H., Sleasman, John W., Rosenberg, Amy S., Kishnani, Priya S.
Format: Artigo
Jezik:Inglês
Izdano: Frontiers Media S.A. 2020
Teme:
Online dostop:https://ncbi.nlm.nih.gov/pmc/articles/PMC7424004/
https://ncbi.nlm.nih.gov/pubmed/32849613
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fimmu.2020.01727
Oznake: Označite
Brez oznak, prvi označite!