Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease

Documenti analoghi

• Characterization of immune response in Cross-Reactive Immunological Material (CRIM)-positive infantile Pompe disease patients treated with enzyme replacement therapy
  di: Desai, Ankit K., et al.
  Pubblicazione: (2019)
• High dose IVIG successfully reduces high rhGAA IgG antibody titers in a CRIM-negative infantile Pompe disease patient
  di: Rairikar, Mugdha, et al.
  Pubblicazione: (2017)
• Clinical laboratory experience of blood CRIM testing in infantile Pompe disease
  di: Bali, Deeksha S., et al.
  Pubblicazione: (2015)
• Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via Newborn Screening: The benefits of early treatment with enzyme replacement therapy and immune tolerance induction
  di: Li, Cindy, et al.
  Pubblicazione: (2021)
• A Race Against Time—Changing the Natural History of CRIM Negative Infantile Pompe Disease
  di: Gupta, Punita, et al.
  Pubblicazione: (2020)