Long term outcome and clinical experience on immune tolerance induction therapies in infantile Pompe disease

Antzeko izenburuak

• Benefits of Prophylactic Short-Course Immune Tolerance Induction in Patients With Infantile Pompe Disease: Demonstration of Long-Term Safety and Efficacy in an Expanded Cohort
  nork: Desai, Ankit K., et al.
  Argitaratua: (2020)
• Cognitive and academic outcomes in long-term survivors of infantile-onset Pompe disease: A longitudinal follow-up
  nork: Spiridigliozzi, Gail A., et al.
  Argitaratua: (2017)
• Successful immune tolerance induction to enzyme replacement therapy in CRIM-negative infantile Pompe disease
  nork: Messinger, Yoav H., et al.
  Argitaratua: (2012)
• Pulmonary Outcome Measures in Long Term Survivors of Infantile Pompe Disease on Enzyme Replacement Therapy: A case series
  nork: ElMallah, Mai K., et al.
  Argitaratua: (2020)
• Enhanced Response to Enzyme Replacement Therapy in Pompe Disease after the Induction of Immune Tolerance
  nork: Sun, Baodong , et al.
  Argitaratua: (2007)