Loading...

Cognitive and academic outcomes in long-term survivors of infantile-onset Pompe disease: A longitudinal follow-up

This study examines the long-term cognitive and academic outcomes of 11 individuals with infantile onset Pompe disease (IOPD) (median age = 11 years, 1 month, range = 5 years, 6 months through 17 years of age) treated with enzyme replacement therapy from an early age. All participants (7 males, 4 fe...

Fuld beskrivelse

Na minha lista:
Bibliografiske detaljer
Udgivet i:Mol Genet Metab
Main Authors: Spiridigliozzi, Gail A., Keeling, Lori A., Stefanescu, Mihaela, Li, Cindy, Austin, Stephanie, Kishnani, Priya S.
Format: Artigo
Sprog:Inglês
Udgivet: 2017
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC5985833/
https://ncbi.nlm.nih.gov/pubmed/28495044
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymgme.2017.04.014
Tags: Tilføj Tag
Ingen Tags, Vær først til at tagge denne postø!