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Advances in oligonucleotide drug delivery

Oligonucleotides can be used to modulate gene expression via a range of processes including RNAi, target degradation by RNase H-mediated cleavage, splicing modulation, non-coding RNA inhibition, gene activation and programmed gene editing. As such, these molecules have potential therapeutic applicat...

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Detalles Bibliográficos
Publicado en:Nat Rev Drug Discov
Main Authors: Roberts, Thomas C., Langer, Robert, Wood, Matthew J. A.
Formato: Artigo
Idioma:Inglês
Publicado: Nature Publishing Group UK 2020
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC7419031/
https://ncbi.nlm.nih.gov/pubmed/32782413
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41573-020-0075-7
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