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Less Is More: Novel Hepatocyte-Targeted siRNA Conjugates for Treatment of Liver-Related Disorders

N-acetyl-galactosamine (GalNAc) conjugation enhances liver specificity for therapeutic oligonucleotides. Here we report on a novel design with improved activity and stability compared with a triantennary design. We applied a versatile monovalent serinol-GalNAc conjugation strategy. First, 1–4 serial...

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Bibliografski detalji
Izdano u:Mol Ther Nucleic Acids
Glavni autori: Weingärtner, Adrien, Bethge, Lucas, Weiss, Lisa, Sternberger, Maria, Lindholm, Marie Wikstrom
Format: Artigo
Jezik:Inglês
Izdano: American Society of Gene & Cell Therapy 2020
Teme:
Online pristup:https://ncbi.nlm.nih.gov/pmc/articles/PMC7321783/
https://ncbi.nlm.nih.gov/pubmed/32590173
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.omtn.2020.05.026
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