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Application of CRISPR/Cas9 to human-induced pluripotent stem cells: from gene editing to drug discovery

Human-induced pluripotent stem cells (hiPSCs) and CRISPR/Cas9 gene editing system represent two instruments of basic and translational research, which both allow to acquire deep insight about the molecular bases of many diseases but also to develop pharmacological research. This review is focused to...

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Dettagli Bibliografici
Pubblicato in:Hum Genomics
Autori principali: De Masi, Claudia, Spitalieri, Paola, Murdocca, Michela, Novelli, Giuseppe, Sangiuolo, Federica
Natura: Artigo
Lingua:Inglês
Pubblicazione: BioMed Central 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7318728/
https://ncbi.nlm.nih.gov/pubmed/32591003
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s40246-020-00276-2
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