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Intrafamilial phenotypic variation in spinocerebellar ataxia type 23

BACKGROUND: Spinocerebellar ataxia type 23 (SCA23) is an autosomal dominant cerebellar ataxia caused by pathogenic variants in the prodynorphin gene (PDYN). The frequency of PDYN variants is reportedly very low (~ 0.1%) in several ataxia cohorts screened to date. CASE PRESENTATIONS: We found five ca...

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Dettagli Bibliografici
Pubblicato in:Cerebellum Ataxias
Autori principali: Satoh, Shunichi, Kondo, Yasufumi, Ohara, Shinji, Yamaguchi, Tomomi, Nakamura, Katsuya, Yoshida, Kunihiro
Natura: Artigo
Lingua:Inglês
Pubblicazione: BioMed Central 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7310450/
https://ncbi.nlm.nih.gov/pubmed/32587707
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s40673-020-00117-x
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