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Gaucher disease: Biochemical and molecular findings in 141 patients diagnosed in Greece

Gaucher disease (GD) is characterized by a marked phenotypic and genetic diversity. It is caused by the functional deficiency of the lysosomal enzyme β-glucocerebrosidase (GCase), which in most instances results from mutations in the GBA1 gene and over 500 different disease causing mutations have be...

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Библиографические подробности
Опубликовано в: :Mol Genet Metab Rep
Главные авторы: Dimitriou, Evangelia, Moraitou, Marina, Cozar, Mónica, Serra-Vinardell, Jenny, Vilageliu, Lluïsa, Grinberg, Daniel, Mavridou, Irene, Michelakakis, Helen
Формат: Artigo
Язык:Inglês
Опубликовано: Elsevier 2020
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC7284128/
https://ncbi.nlm.nih.gov/pubmed/32547927
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymgmr.2020.100614
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