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The Spectrum of Krabbe Disease in Greece: Biochemical and Molecular Findings

Krabbe disease is an autosomal recessive neurodegenerative lysosomal storage disease caused by the deficiency of β-galactocerebrosidase. This deficiency results in the impaired degradation of β-galactocerebroside, a major myelin lipid, and of galactosylsphingosine. Based on the age of onset of neuro...

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Detaylı Bibliyografya
Yayımlandı:JIMD Rep
Asıl Yazarlar: Dimitriou, Evangelia, Cozar, Monica, Mavridou, Irene, Grinberg, Daniel, Vilageliu, Lluïsa, Michelakakis, Helen
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: Springer Berlin Heidelberg 2015
Konular:
Online Erişim:https://ncbi.nlm.nih.gov/pmc/articles/PMC5059214/
https://ncbi.nlm.nih.gov/pubmed/26108647
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2015_457
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