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MR biomarkers predict clinical function in Duchenne muscular dystrophy

OBJECTIVE: To investigate the potential of lower extremity magnetic resonance (MR) biomarkers to serve as endpoints in clinical trials of therapeutics for Duchenne muscular dystrophy (DMD) by characterizing the longitudinal progression of MR biomarkers over 48 months and assessing their relationship...

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Dades bibliogràfiques
Publicat a:Neurology
Autors principals: Barnard, Alison M., Willcocks, Rebecca J., Triplett, William T., Forbes, Sean C., Daniels, Michael J., Chakraborty, Saptarshi, Lott, Donovan J., Senesac, Claudia R., Finanger, Erika L., Harrington, Ann T., Tennekoon, Gihan, Arora, Harneet, Wang, Dah-Jyuu, Sweeney, H. Lee, Rooney, William D., Walter, Glenn A., Vandenborne, Krista
Format: Artigo
Idioma:Inglês
Publicat: Lippincott Williams & Wilkins 2020
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC7238941/
https://ncbi.nlm.nih.gov/pubmed/32024675
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1212/WNL.0000000000009012
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