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MR biomarkers predict clinical function in Duchenne muscular dystrophy

OBJECTIVE: To investigate the potential of lower extremity magnetic resonance (MR) biomarkers to serve as endpoints in clinical trials of therapeutics for Duchenne muscular dystrophy (DMD) by characterizing the longitudinal progression of MR biomarkers over 48 months and assessing their relationship...

Täydet tiedot

Tallennettuna:
Bibliografiset tiedot
Julkaisussa:Neurology
Päätekijät: Barnard, Alison M., Willcocks, Rebecca J., Triplett, William T., Forbes, Sean C., Daniels, Michael J., Chakraborty, Saptarshi, Lott, Donovan J., Senesac, Claudia R., Finanger, Erika L., Harrington, Ann T., Tennekoon, Gihan, Arora, Harneet, Wang, Dah-Jyuu, Sweeney, H. Lee, Rooney, William D., Walter, Glenn A., Vandenborne, Krista
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: Lippincott Williams & Wilkins 2020
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC7238941/
https://ncbi.nlm.nih.gov/pubmed/32024675
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1212/WNL.0000000000009012
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