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Modeling disease trajectory in Duchenne muscular dystrophy

OBJECTIVE: To quantify disease progression in individuals with Duchenne muscular dystrophy (DMD) using magnetic resonance biomarkers of leg muscles. METHODS: MRI and magnetic resonance spectroscopy (MRS) biomarkers were acquired from 104 participants with DMD and 51 healthy controls using a prospect...

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Bibliografiske detaljer
Udgivet i:Neurology
Main Authors: Rooney, William D., Berlow, Yosef A., Triplett, William T., Forbes, Sean C., Willcocks, Rebecca J., Wang, Dah-Jyuu, Arpan, Ishu, Arora, Harneet, Senesac, Claudia, Lott, Donovan J., Tennekoon, Gihan, Finkel, Richard, Russman, Barry S., Finanger, Erika L., Chakraborty, Saptarshi, O'Brien, Elliott, Moloney, Brendan, Barnard, Alison, Sweeney, H. Lee, Daniels, Michael J., Walter, Glenn A., Vandenborne, Krista
Format: Artigo
Sprog:Inglês
Udgivet: Lippincott Williams & Wilkins 2020
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Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC7251517/
https://ncbi.nlm.nih.gov/pubmed/32184340
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1212/WNL.0000000000009244
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