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Single-Cell Transcriptome Analysis of Mouse Liver Cell-Specific Tropism and Transcriptional Dysregulation Following Intravenous Administration of AAVrh.10 Vectors

Capitalizing on liver tropism of adeno-associated viral (AAV) vectors, intravenous vector administration is commonly used to genetically modify hepatocytes, a strategy currently in clinical trials for a number of liver-based hereditary disorders. Although hepatocytes are known to exhibit extensive p...

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Detalles Bibliográficos
Publicado en:Hum Gene Ther
Main Authors: Zhu, Detu, Rostami, Mahboubeh R., Zuo, Wu-lin, Leopold, Philip L., Crystal, Ronald G.
Formato: Artigo
Idioma:Inglês
Publicado: Mary Ann Liebert, Inc., publishers 2020
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC7232697/
https://ncbi.nlm.nih.gov/pubmed/32143547
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2019.366
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