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ATP6AP1‐CDG: Follow‐up and female phenotype

In 2016, 11 male patients were reported with immunodeficiency and hepatic, gastric and (in some) neurological disease due to X‐linked ATP6AP1 deficiency (ATP6AP1‐CDG). In 2018, three other patients were reported with additional features: connective tissue abnormalities, sensorineural hearing loss, h...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:JIMD Rep
Egile Nagusiak: Lipiński, Patryk, Rokicki, Dariusz, Bogdańska, Anna, Lesiak, Justyna, Lefeber, Dirk J., Tylki‐Szymańska, Anna
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: John Wiley & Sons, Inc. 2020
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC7203642/
https://ncbi.nlm.nih.gov/pubmed/32395412
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jmd2.12104
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