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ATP6AP1‐CDG: Follow‐up and female phenotype

In 2016, 11 male patients were reported with immunodeficiency and hepatic, gastric and (in some) neurological disease due to X‐linked ATP6AP1 deficiency (ATP6AP1‐CDG). In 2018, three other patients were reported with additional features: connective tissue abnormalities, sensorineural hearing loss, h...

Täydet tiedot

Tallennettuna:
Bibliografiset tiedot
Julkaisussa:JIMD Rep
Päätekijät: Lipiński, Patryk, Rokicki, Dariusz, Bogdańska, Anna, Lesiak, Justyna, Lefeber, Dirk J., Tylki‐Szymańska, Anna
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: John Wiley & Sons, Inc. 2020
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC7203642/
https://ncbi.nlm.nih.gov/pubmed/32395412
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jmd2.12104
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