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G-CSF (filgrastim) treatment for amyotrophic lateral sclerosis: protocol for a phase II randomised, double-blind, placebo-controlled, parallel group, multicentre clinical study (STEMALS-II trial)

INTRODUCTION: Amyotrophic lateral sclerosis (ALS) is a fatal progressive neurological disorder characterised by a selective degeneration of motor neurons (MNs). Stem cell transplantation is considered as a promising strategy in neurological disorders therapy and the possibility of inducing bone marr...

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Pubblicato in:BMJ Open
Autori principali: Salamone, Paolina, Fuda, Giuseppe, Casale, Federico, Marrali, Giuseppe, Lunetta, Christian, Caponnetto, Claudia, Mazzini, Letizia, La Bella, Vincenzo, Mandrioli, Jessica, Simone, Isabella Laura, Moglia, Cristina, Calvo, Andrea, Tarella, Corrado, Chio, Adriano
Natura: Artigo
Lingua:Inglês
Pubblicazione: BMJ Publishing Group 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7202695/
https://ncbi.nlm.nih.gov/pubmed/32209625
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1136/bmjopen-2019-034049
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