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CRISPR-Generated Animal Models of Duchenne Muscular Dystrophy

Duchenne muscular dystrophy (DMD) is a fatal X-linked recessive neuromuscular disorder most commonly caused by mutations disrupting the reading frame of the dystrophin (DMD) gene. DMD codes for dystrophin, which is critical for maintaining the integrity of muscle cell membranes. Without dystrophin,...

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Dades bibliogràfiques
Publicat a:Genes (Basel)
Autors principals: Lim, Kenji Rowel Q., Nguyen, Quynh, Dzierlega, Kasia, Huang, Yiqing, Yokota, Toshifumi
Format: Artigo
Idioma:Inglês
Publicat: MDPI 2020
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC7141101/
https://ncbi.nlm.nih.gov/pubmed/32213923
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/genes11030342
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