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Changing Times for CLN2 Disease: The Era of Enzyme Replacement Therapy

Neuronal ceroid lipofuscinosis type 2 (CLN2 disease) is a progressive neurodegenerative disease that results in early-onset, severe, progressive, neurological disabilities, leading to death in late childhood or early adolescence. Management has relied on symptomatic care, and supportive and palliati...

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Podrobná bibliografie
Vydáno v:Ther Clin Risk Manag
Hlavní autoři: Specchio, Nicola, Pietrafusa, Nicola, Trivisano, Marina
Médium: Artigo
Jazyk:Inglês
Vydáno: Dove 2020
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC7127909/
https://ncbi.nlm.nih.gov/pubmed/32280231
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.2147/TCRM.S241048
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