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Cell-penetrating peptide-conjugated antisense oligonucleotides restore systemic muscle and cardiac dystrophin expression and function

Antisense oligonucleotides (AOs) have the potential to induce functional dystrophin protein expression via exon skipping by restoring in-frame transcripts in the majority of patients suffering from Duchenne muscular dystrophy (DMD). AOs of morpholino phosphoroamidate (PMO) and 2′-O-methyl phosphorot...

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Detalhes bibliográficos
Publicado no:Hum Mol Genet
Main Authors: Yin, HaiFang, Moulton, Hong M., Seow, Yiqi, Boyd, Corinne, Boutilier, Jordan, Iverson, Patrick, Wood, Matthew J.A.
Formato: Artigo
Idioma:Inglês
Publicado em: Oxford University Press 2008
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7108561/
https://ncbi.nlm.nih.gov/pubmed/18784278
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddn293
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