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Structure-Specific Cleavage of an RNA Repeat Expansion with a Dimeric Small Molecule Is Advantageous over Sequence-Specific Recognition by an Oligonucleotide

Myotonic dystrophy type 2 (DM2) is a genetically defined muscular dystrophy that is caused by an expanded repeat of r(CCUG) [r(CCUG)(exp)] in intron 1 of a CHC-type zinc finger nucleic acid binding protein (CNBP) pre-mRNA. Various mechanisms contribute to DM2 pathology including pre-mRNA splicing de...

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Detalhes bibliográficos
Publicado no:ACS Chem Biol
Main Authors: Benhamou, Raphael I., Angelbello, Alicia J., Andrews, Ryan J., Wang, Eric T., Moss, Walter N., Disney, Matthew D.
Formato: Artigo
Idioma:Inglês
Publicado em: 2020
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7081929/
https://ncbi.nlm.nih.gov/pubmed/31927948
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1021/acschembio.9b00958
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