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Clinical and Radiologic Evaluation of an Individual with Hypochondroplasia and a Novel FGFR3 Mutation

Hypochondroplasia (HCH), a skeletal dysplasia caused by mutations in the fibroblast growth factor receptor 3 ( FGFR3 ) gene, is characterized by disproportionate short stature. The p.Asn540Lys (p.N540K) mutation accounts for ∼50 to 70% of cases of HCH, but novel FGFR3 mutations are described. We pre...

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Publicat a:J Pediatr Genet
Autors principals: Ramos Mejía, Rosario, Aza-Carmona, Miriam, del Pino, Mariana, Heath, Karen E., Fano, Virginia, Obregon, Maria Gabriela
Format: Artigo
Idioma:Inglês
Publicat: Georg Thieme Verlag KG 2020
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6976309/
https://ncbi.nlm.nih.gov/pubmed/31976144
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1055/s-0039-1695056
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